Rare Diseases Conferences | Infectious Diseases | Rare Diseases 2024 | Orphan Drugs | Amsterdam | Netherlands | Europe | Conference Series

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Rare Diseases Congress 2025

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Market Analysis

The global orphan drugs market size was valued at USD 170.49 billion in 2023. The market is projected to grow from USD 189.17 billion in 2024 to USD 468.58 billion by 2032, exhibiting a CAGR of 12.0% during the forecast period. North America dominated the global market with a share of 53.94% in 2023.

Orphan drugs are developed by the pharmaceutical industry for economic reasons but respond to the public health needs. These drugs are developed to treat patients suffering from serious diseases for which no treatment, or at least a satisfactory one, has so far been available. For instance, an article published by the Orphanet in 2023 stated that the number of rare diseases for which no treatment is currently available is estimated to be between 4,000 and 5,000 globally. Moreover, 25 to 30 million people are reported to be affected by these rare diseases in Europe.

According to the European Organization for Rare Diseases, orphan drugs are produced for diagnosis, prevention, and treatment of rare disorders. The oncology therapy area holds a considerably higher share in the global market due to emergence of new cancer-related diseases. Additionally, FDA approvals to a series of cancer-related orphan drugs are expected to result in increased commercialization of these drugs, especially in the oncology therapy area, during the forecast period. The market will derive growth from higher demand for immunomodulators, as they regularize or amplify the immune system. Rising prevalence of infectious diseases in developed as well as emerging nations and higher prices of medications are projected to fuel the demand for immunomodulators, thus contributing to the global orphan drugs market growth during the forecast period.

The COVID-19 pandemic had a positive impact on the market growth due to an increase in regulatory approvals. In 2021, the growth of the market continued primarily due to the resumption of research and development activities of market players. This growth is expected to continue during the forecast period, owing to the launch of various pipeline candidates for various indications by key players. Such trends indicate that the market is poised for steady growth during the forecast period.

ORPHAN DRUGS MARKET TRENDS:

One of the prominent trends in the global market is strong product launches for these disease indications. Globally, patients suffering from rare diseases are seeking efficient and potent treatment for these disorders. Increasing R&D initiatives and rising advocacy by patients’ groups for effective treatment are propelling the introduction of newer and more effective product offerings. These trends have led to the development and marketing of several blockbuster drugs for the treatment of many types of cancers, immunological diseases, and other rare disorders.

As per the Orphan Drug Report 2022 by Evaluate Pharma, it is estimated that the rise of top 10 orphan drugs blockbusters will be worth between USD 3.0 billion and USD 13 billion by 2026. Furthermore, it estimated that 40% of Johnson & Johnson’s pharmaceutical sales will come from orphan drugs, especially through blood cancer drugs, such as Imbruvica and Darzalex, which is expected to be worth over USD 23.0 billion by 2026. Thus, the introduction of such sophisticated orphan therapeutics by established and emerging companies have been instrumental in boosting the adoption of these drugs, which is expected to aid the growth of the global market during the forecast period.

To Collaborate Scientific Professionals around the World

Conference Date June 02-03, 2025

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Keytopics

  • Inherited Diseases
  • Access To Orphan Drugs
  • Autoimmune Diseases
  • Clinical Trials For Rare Diseases
  • Diagnostic Challenges
  • Genetic Disorders
  • Genetic Mutations
  • Metabolic Disorders
  • Neuromuscular Diseases
  • Orphan Drug Development
  • Patient Advocacy
  • Personalized Medicine
  • Rare Cancers
  • Rare Pediatric Conditions
  • Regulatory Policies
  • Treatment Innovations